My Nonprofit Reviews

FRAXA has been a remarkable force working for improved treatments for fragile X. The Foundation has pioneered community based drug development in the field of rare diseases and isn't just advocating for a cure, it's actually directing the process of drug discovery. FRAXA funds basic research that helps us understand the mechanisms of disease in fragile X; 28 years' worth of this work has led to the discovery of many drug targets. The FRAXA Drug Validation Initiative tests promising new treatments in animal models, and this has led to many clinical trials around the world. The most recent trials have been the most successful ever, and new treatments are likely coming very soon!