Andrew's Buddies Corporation Overview
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Geographic areas served: International
Programs: In July 2010, FightSMA announced a new fundraising campaign for spinal muscular atrophy (SMA) gene therapy, “Realizing the Dream.” FightSMA is collaborating with the Santa Barbara-based Gwendolyn Strong Foundation, to form a bi-coastal partnership with a common goal: to bring SMA gene therapy to clinical trial.
FightSMA’s objective for the balance of 2010 is to complete funding for Phase One ($250,000) and then for Year-One of Phase Two of the research program. “The first objective is to build a solid foundation of safety and to eliminate toxicity,” said Dr. Chris Lorson, FightSMA Science Director. Additionally, FightSMA plans to raise another $250,000 to fund the first year of Phase Two (Delivery & Efficacy). The “Realizing the Dream” program will be accomplished through a series of campaigns. Completing these two Phases will bring SMA gene therapy significantly closer to clinical trial.
To learn more about gene therapy and how to become more involved in "Realizing the Dream," visit www.FightSMA.org.